A translational approach for limb vascular delivery of the micro-dystrophin gene without high volume or high pressure for treatment of Duchenne muscular dystrophy

A translational approach for limb vascular delivery of the micro-dystrophin gene without high volume or high pressure for treatment of Duchenne muscular dystrophy

<p>Abstract</p> <p>Background</p> <p>Duchenne muscular dystrophy (DMD) is an X-linked recessive disorder with monogenic mutations setting the stage for successful gene therapy treatment. We have completed a study that directly deals with the following key issues that ca...

Full description

Bibliographic Details
Main Authors: Chicoine Louis G, Coley Brian D, Montgomery Chrystal L, Janssen Paul ML, Rodino-Klapac Louise R, Clark K Reed, Mendell Jerry R
Format: Article
Language:English
Published: BMC 2007-09-01
Series:Journal of Translational Medicine
Online Access:http://www.translational-medicine.com/content/5/1/45

Internet

http://www.translational-medicine.com/content/5/1/45

Similar Items