Whole‐blood dysregulation of actin‐cytoskeleton pathway in adult spinal muscular atrophy patients

Abstract Objective Recent advances in therapeutics have improved prognosis for severely affected spinal muscular atrophy (SMA) type 1 and 2 patients, while the best method of treatment for SMA type 3 patients with later onset of disease is unknown. To better characterize the SMA type 3 population an...

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Bibliographic Details
Main Authors: Jennifer J. Siranosian, Flavia C. Nery, Christiano R. R. Alves, Benjamin A. Siranosian, Nicholas J. Lyons, Eric J. Eichelberger, Reid Garner, Salomé Da Silva Duarte Lepez, Alec J. Johnstone, Aravind Subramanian, Kathryn J. Swoboda
Format: Article
Language:English
Published: Wiley 2020-07-01
Series:Annals of Clinical and Translational Neurology
Online Access:https://doi.org/10.1002/acn3.51092