Search Results - Anna Villa
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Development of central nervous system autoimmunity is impaired in the absence of Wiskott-Aldrich syndrome protein. by Marita Bosticardo, Silvia Musio, Elena Fontana, Stefano Angiari, Elena Draghici, Gabriela Constantin, Pietro L Poliani, Rosetta Pedotti, Anna Villa
Published in PLoS ONE (2014-01-01)Get full text
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RANKL Cytokine: From Pioneer of the Osteoimmunology Era to Cure for a Rare Disease by Nadia Lo Iacono, Alessandra Pangrazio, Mario Abinun, Robbert Bredius, Marco Zecca, Harry C. Blair, Paolo Vezzoni, Anna Villa, Cristina Sobacchi
Published in Clinical and Developmental Immunology (2013-01-01)Get full text
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3
P1405: IN-DEPTH GENOME INTEGRITY EVALUATION AND GMP-COMPLIANT MANUFACTURING OF HDR GENE EDITED CD4+ T CELLS FOR THE TREATMENT OF HYPER IGM 1 by Daniele Canarutto, Claudia Asperti, Valentina Vavassori, Simona Porcellini, Elisabetta Rovelli, Marianna Paulis, Samuele Ferrari, Tiziana Plati, Lucia Sergi Sergi, Anna Villa, Marina Radrizzani, Luigi Naldini
Published in HemaSphere (2023-08-01)Get full text
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4
MicroRNA-127-3p controls murine hematopoietic stem cell maintenance by limiting differentiation by Laura Crisafulli, Sharon Muggeo, Paolo Uva, Yulei Wang, Masayuki Iwasaki, Silvia Locatelli, Achille Anselmo, Federico S. Colombo, Carmelo Carlo-Stella, Michael L. Cleary, Anna Villa, Bernhard Gentner, Francesca Ficara
Published in Haematologica (2019-09-01)Get full text
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Partial correction of immunodeficiency by lentiviral vector gene therapy in mouse models carrying Rag1 hypomorphic mutations by Maria Carmina Castiello, Maria Carmina Castiello, Martina Di Verniere, Martina Di Verniere, Elena Draghici, Elena Fontana, Elena Fontana, Sara Penna, Lucia Sereni, Alessandra Zecchillo, Alessandra Zecchillo, Denise Minuta, Paolo Uva, Marco Zahn, Irene Gil-Farina, Andrea Annoni, Silvia Iaia, Lisa M. Ott de Bruin, Lisa M. Ott de Bruin, Luigi D. Notarangelo, Karin Pike-Overzet, Frank J. T. Staal, Anna Villa, Anna Villa, Valentina Capo, Valentina Capo
Published in Frontiers in Immunology (2023-11-01)Get full text
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Correction of osteopetrosis in the neonate oc/oc murine model after lentiviral vector gene therapy and non-genotoxic conditioning by Sara Penna, Alessandra Zecchillo, Alessandra Zecchillo, Martina Di Verniere, Elena Fontana, Elena Fontana, Valeria Iannello, Valeria Iannello, Eleonora Palagano, Eleonora Palagano, Stefano Mantero, Stefano Mantero, Andrea Cappelleri, Andrea Cappelleri, Elena Rizzoli, Elena Rizzoli, Ludovica Santi, Laura Crisafulli, Laura Crisafulli, Marta Filibian, Antonella Forlino, Luca Basso-Ricci, Serena Scala, Eugenio Scanziani, Eugenio Scanziani, Thorsten Schinke, Francesca Ficara, Francesca Ficara, Cristina Sobacchi, Cristina Sobacchi, Anna Villa, Anna Villa, Valentina Capo, Valentina Capo
Published in Frontiers in Endocrinology (2024-09-01)Get full text
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Targeted Gene Correction in Osteopetrotic-Induced Pluripotent Stem Cells for the Generation of Functional Osteoclasts by Tui Neri, Sharon Muggeo, Marianna Paulis, Maria Elena Caldana, Laura Crisafulli, Dario Strina, Maria Luisa Focarelli, Francesca Faggioli, Camilla Recordati, Samantha Scaramuzza, Eugenio Scanziani, Stefano Mantero, Chiara Buracchi, Cristina Sobacchi, Angelo Lombardo, Luigi Naldini, Paolo Vezzoni, Anna Villa, Francesca Ficara
Published in Stem Cell Reports (2015-10-01)Get full text
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Scalable GMP-compliant gene correction of CD4+ T cells with IDLV template functionally validated in vitro and in vivo by Claudia Asperti, Daniele Canarutto, Simona Porcellini, Francesca Sanvito, Francesca Cecere, Valentina Vavassori, Samuele Ferrari, Elisabetta Rovelli, Luisa Albano, Aurelien Jacob, Lucia Sergi Sergi, Elisa Montaldo, Francesca Ferrua, Luis Ignacio González-Granado, Vassilios Lougaris, Raffaele Badolato, Andrea Finocchi, Anna Villa, Marina Radrizzani, Luigi Naldini
Published in Molecular Therapy: Methods & Clinical Development (2023-09-01)Get full text
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9
Autoimmunity in thymic epithelial tumors: a not yet clarified pathologic paradigm associated with several unmet clinical needs by Matteo Perrino, Emanuele Voulaz, Emanuele Voulaz, Simone Balin, Gerardo Cazzato, Elena Fontana, Elena Fontana, Sara Franzese, Sara Franzese, Martina Defendi, Martina Defendi, Fabio De Vincenzo, Nadia Cordua, Roberto Tamma, Federica Borea, Federica Borea, Marta Aliprandi, Marta Aliprandi, Marco Airoldi, Marco Airoldi, Luigi Giovanni Cecchi, Luigi Giovanni Cecchi, Roberta Fazio, Roberta Fazio, Marco Alloisio, Marco Alloisio, Giuseppe Marulli, Giuseppe Marulli, Armando Santoro, Armando Santoro, Luca Di Tommaso, Luca Di Tommaso, Giuseppe Ingravallo, Laura Russo, Giorgio Da Rin, Anna Villa, Anna Villa, Silvia Della Bella, Silvia Della Bella, Paolo Andrea Zucali, Paolo Andrea Zucali, Domenico Mavilio, Domenico Mavilio
Published in Frontiers in Immunology (2024-04-01)Get full text
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Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome by Valentina Vavassori, Elisabetta Mercuri, Genni E Marcovecchio, Maria C Castiello, Giulia Schiroli, Luisa Albano, Carrie Margulies, Frank Buquicchio, Elena Fontana, Stefano Beretta, Ivan Merelli, Andrea Cappelleri, Paola MV Rancoita, Vassilios Lougaris, Alessandro Plebani, Maria Kanariou, Arjan Lankester, Francesca Ferrua, Eugenio Scanziani, Cecilia Cotta‐Ramusino, Anna Villa, Luigi Naldini, Pietro Genovese
Published in EMBO Molecular Medicine (2021-01-01)Get full text
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Expanded circulating hematopoietic stem/progenitor cells as novel cell source for the treatment of TCIRG1 osteopetrosis by Valentina Capo, Sara Penna, Ivan Merelli, Matteo Barcella, Serena Scala, Luca Basso-Ricci, Elena Draghici, Eleonora Palagano, Erika Zonari, Giacomo Desantis, Paolo Uva, Roberto Cusano, Lucia Sergi Sergi, Laura Crisafulli, Despina Moshous, Polina Stepensky, Katarzyna Drabko, Zühre Kaya, Ekrem Unal, Alper Gezdirici, Giuseppe Menna, Marta Serafini, Alessandro Aiuti, Silvia Laura Locatelli, Carmelo Carlo-Stella, Ansgar S. Schulz, Francesca Ficara, Cristina Sobacchi, Bernhard Gentner, Anna Villa
Published in Haematologica (2020-01-01)Get full text
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