Search Results - E.J. van Beers

P1735: IMPROVEMENTS IN PATIENT-REPORTED OUTCOMES IN MITAPIVAT-TREATED PATIENTS WITH PYRUVATE KINASE DEFICIENCY: A DESCRIPTIVE ANALYSIS FROM THE PHASE 3 ACTIVATE TRIAL by K. H. Kuo, R. F. Grace, E. J. van Beers, W. Barcellini, A. Glenthøj, S. Holzhauer, P. Patel, V. Beynon, J. Li, E. Zagadailov, H. Al-Samkari

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P1542: COMORBIDITIES AND COMPLICATIONS ACROSS GENOTYPES IN ADULT PATIENTS WITH PYRUVATE KINASE DEFICIENCY: ANALYSIS FROM THE PEAK REGISTRY by A. Glenthøj, R. F. Grace, E. J. van Beers, J.-L. Vives Corrons, B. Glader, K. H. M. Kuo, C. Lander, D. Pospíŝilová, J. Williams, Y. Yan, B. McGee, P. Bianchi

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No association of the hypercoagulable state with sickle cell disease related pulmonary hypertension by E.J. van Beers, H.M.H. Spronk, H. ten Cate, A.J. Duits, D.P.M. Brandjes, J.W.J. van Esser, B.J. Biemond, J.B. Schnog, on behalf of the CURAMA study Group

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P1565: MITAPIVAT IMPROVES INEFFECTIVE ERYTHROPOIESIS AND REDUCES IRON OVERLOAD IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY by E. J. van Beers, H. Al-Samkari, R. F. Grace, W. Barcellini, A. Glenthøj, M. P. Judge, P. A. Kosinski, R. Xu, V. Beynon, B. McGee, J. B. Porter, K. H. M. Kuo

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P1562: CHARACTERIZING IRON OVERLOAD BY AGE IN PATIENTS DIAGNOSED WITH PYRUVATE KINASE DEFICIENCY – A DESCRIPTIVE ANALYSIS FROM THE PEAK REGISTRY by P. Bianchi, R. F. Grace, J.-L. Vives Corrons, B. Glader, A. Glenthøj, H. Kanno, K. H. Kuo, C. Lander, D. M. Layton, D. Pospíŝilová, V. Viprakasit, J. Williams, Y. Yan, B. McGee, E. J. van Beers

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P1548: LONG-TERM TREATMENT WITH ORAL MITAPIVAT IS ASSOCIATED WITH NORMALIZATION OF HEMOGLOBIN LEVELS IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY by W. Barcellini, R. F. Grace, H. Al-Samkari, A. Glenthøj, J. A. Rothman, M. Morado Arias, D. M. Layton, O. Andres, M. DiBacco, P. Hawkins, M. P. Judge, F. Tai, J. Morales-Arias, V. Beynon, E. J. van Beers

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P1065: CONGENITAL ERYTHROCYTOSIS DUE TO HETEROZYGOUS VARIANTS IN THE BISPHOSPHOGLYCERATE MUTASE GENE by M. J. van Dijk, B. A. van Oirschot, M. C. Stam-Slob, B. van der Zwaag, E. J. van Beers, J. J. Jans, P. van der Linden, J. M. Torregrosa Diaz, B. Gardie, F. Girodon, R. Schots, N. Thielen, R. van Wijk

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P1501: FOLLOW-UP RESULTS OF A PHASE 2 STUDY ASSESSING THE SAFETY AND EFFICACY OF MITAPIVAT TREATMENT, AN ORAL PYRUVATE KINASE ACTIVATOR, FOR UP TO 60 WEEKS IN SUBJECTS WITH SICKLE... by M. J. van Dijk, M. A. Rab, B. A. van Oirschot, J. Bos, C. Derichs, A. W. Rijneveld, M. H. Cnossen, E. Nur, B. J. Biemond, M. Bartels, J. J. Jans, W. W. van Solinge, R. E. Schutgens, R. van Wijk, E. J. van Beers

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P1544: BONE MINERAL DENSITY REMAINS STABLE IN PYRUVATE KINASE DEFICIENCY PATIENTS RECEIVING LONG-TERM TREATMENT WITH MITAPIVAT by H. Al-Samkari, R. F. Grace, A. Glenthøj, O. Andres, W. Barcellini, F. Galactéros, K. H. M. Kuo, D. M. Layton, M. Morado Arias, V. Viprakasit, Y. Dong, F. Tai, L. Grekas, K. Khoja, S. Gheuens, B. McGee, J. B. Porter, E. J. van Beers

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5589320 FOLLOW-UP RESULTS OF A PHASE 2 STUDY ASSESSING THE SAFETY AND EFFICACY OF MITAPIVAT TREATMENT, AN ORAL PYRUVATE KINASE ACTIVATOR, FOR UP TO 60 WEEKS IN SUBJECTS WITH SICKLE... by M.J. van Dijk, M.A.E. Rab, B.A. van Oirschot, J.F. Bos, C. Derichs, A.W. Rijneveld, M.H. Cnossen, E. Nur, B.J. Biemond, M. Bartels, J.J.M. Jans, W.W. van Solinge, R.E.G. Schutgens, R. van Wijk, E.J. van Beers

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P1545: DURABILITY OF HEMOGLOBIN RESPONSE AND REDUCTION IN TRANSFUSION BURDEN IS MAINTAINED OVER TIME IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY TREATED WITH MITAPIVAT IN A LONG-TE... by R. F. Grace, A. Glenthøj, W. Barcellini, M. Verhovsek, J. A. Rothman, M. Morado Arias, D. M. Layton, O. Andres, F. Galactéros, E. J. van Beers, K. Onodera, V. Viprakasit, S. Chonat, J. B. Porter, M. P. Judge, P. A. Kosinski, P. Hawkins, S. Gheuens, R. Xu, B. McGee, V. Beynon, H. Al-Samkari

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