Search Results - F Peyvandi
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EFFICACY AND SAFETY OF VALOCTOCOGENE ROXAPARVOVEC 4 YEARS AFTER GENE TRANSFER IN GENER8-1 by MC Ozelo, AD Leavitt, J Mahlangu, G Kenet, SW Pipe, S Chou, R Klamroth, F Peyvandi, T Robinson, GT Group
Published in Hematology, Transfusion and Cell Therapy (2024-10-01)Get full text
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A SIMULATION STUDY TO PROVIDE GUIDANCE FOR INDIVIDUALS TRANSITIONING FROM EMICIZUMAB TO VALOCTOCOGENE ROXAPARVOVEC by W Kuwabara, D Osmond, J Henshaw, S Agarwal, V Newman, C Hermans, W Miesbach, S Pipe, RS Jr, F Peyvandi
Published in Hematology, Transfusion and Cell Therapy (2023-10-01)Get full text
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BLEEDING, FVIII ACTIVITY, AND SAFETY 3 YEARS AFTER GENE TRANSFER WITH VALOCTOCOGENE ROXAPARVOVEC: RESULTS FROM GENER8-1 by MC Ozelo, J Mahlangu, B Madan, J Mason, F Peyvandi, AV Drygalski, G Yamaguti-Hayakawa, TM Robinson, SW Pipe, TT Gener-Eigh
Published in Hematology, Transfusion and Cell Therapy (2023-10-01)Get full text
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OUTCOMES OF PATIENTS WITH WORSENING ACQUIRED THROMBOTIC THROMBOCYTOPENIC PURPURA (TTP) DESPITE DAILY THERAPEUTIC PLASMA EXCHANGE IN THE PHASE 3 HERCULES TRIAL by M. Scully, J.L. Rubia, F. Peyvandi, S. Cataland, P. Coppo, J.A.K. Hovinga, P. Knoebl, K. Pavenski, F. Callewaert, J.M.M. Edou, R.P. Sousa
Published in Hematology, Transfusion and Cell Therapy (2020-11-01)Get full text
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S294: LONG-TERM SAFETY AND EFFICACY OF CAPLACIZUMAB FOR ACQUIRED THROMBOTIC THROMBOCYTOPENIC PURPURA (ATTP): THE POST-HERCULES STUDY by M. Scully, J. de la Rubia, K. Pavenski, A. Metjian, P. Knöbl, F. Peyvandi, S. Cataland, P. Coppo, J. A. Kremer Hovinga, R. De Passos Sousa, F. Callewaert, S. Gunawardena, J. Lin
Published in HemaSphere (2022-06-01)Get full text
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Reduced circulating FABP2 in patients with moderate to severe COVID-19 may indicate enterocyte functional change rather than cell death by G. Assante, A. Tourna, R. Carpani, F. Ferrari, D. Prati, F. Peyvandi, F. Blasi, A. Bandera, A. Le Guennec, S. Chokshi, V. C. Patel, I. J. Cox, L. Valenti, N. A. Youngson
Published in Scientific Reports (2022-11-01)Get full text
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Thrombotic thrombocytopenic purpura and defective apoptosis due to CASP8/10 mutations: the role of mycophenolate mofetil by F. Fioredda, E. Cappelli, A. Mariani, A. Beccaria, E. Palmisani, A. Grossi, I. Ceccherini, R. Venè, C. Micalizzi, M. Calvillo, F. Pierri, I. Mancini, F. Peyvandi, F. Corsolini, C. Dufour, M. Miano
Published in Blood Advances (2019-11-01)Get full text
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