Search Results - Giuliana Ferrari
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The GATA1-HS2 enhancer allows persistent and position-independent expression of a β-globin transgene. by Annarita Miccio, Valentina Poletti, Valentina Poletti, Francesca Tiboni, Claudia Rossi, Antonella Antonelli, Fulvio Mavilio, Giuliana Ferrari
Published in PLoS ONE (2011-01-01)Get full text
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The EHA Research Roadmap: Hematopoietic Stem Cell Gene Therapy by Luigi Naldini, Maria Pia Cicalese, Maria Ester Bernardo, Bernhard Gentner, Michela Gabaldo, Giuliana Ferrari, Alessandro Aiuti
Published in HemaSphere (2022-02-01)Get full text
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Transcription factor binding sites are genetic determinants of retroviral integration in the human genome. by Barbara Felice, Claudia Cattoglio, Davide Cittaro, Anna Testa, Annarita Miccio, Giuliana Ferrari, Lucilla Luzi, Alessandra Recchia, Fulvio Mavilio
Published in PLoS ONE (2009-01-01)Get full text
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Efficient Ex Vivo Engineering and Expansion of Highly Purified Human Hematopoietic Stem and Progenitor Cell Populations for Gene Therapy by Erika Zonari, Giacomo Desantis, Carolina Petrillo, Francesco E. Boccalatte, Maria Rosa Lidonnici, Anna Kajaste-Rudnitski, Alessandro Aiuti, Giuliana Ferrari, Luigi Naldini, Bernhard Gentner
Published in Stem Cell Reports (2017-04-01)Get full text
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NCOA4-mediated ferritinophagy in macrophages is crucial to sustain erythropoiesis in mice by Antonella Nai, Maria Rosa Lidonnici, Giorgia Federico, Mariateresa Pettinato, Violante Olivari, Federica Carrillo, Simonetta Geninatti Crich, Giuliana Ferrari, Clara Camaschella, Laura Silvestri, Francesca Carlomagno
Published in Haematologica (2020-02-01)Get full text
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Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies by Mégane Brusson, Anne Chalumeau, Pierre Martinucci, Oriana Romano, Tristan Felix, Valentina Poletti, Samantha Scaramuzza, Sophie Ramadier, Cecile Masson, Giuliana Ferrari, Fulvio Mavilio, Marina Cavazzana, Mario Amendola, Annarita Miccio
Published in Molecular Therapy: Nucleic Acids (2023-06-01)Get full text
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Transient decrease of serum iron after acute erythropoietin treatment contributes to hepcidin inhibition by ERFE in mice by Irene Artuso, Mariateresa Pettinato, Antonella Nai, Alessia Pagani, Ugo Sardo, Benjamin Billoré, Maria Rosa Lidonnici, Cavan Bennett, Giacomo Mandelli, Sant-Rayn Pasricha, Giuliana Ferrari, Clara Camaschella, Léon Kautz, Laura Silvestri
Published in Haematologica (2019-03-01)Get full text
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Quantitatively different red cell/nucleated cell chimerism in patients with long-term, persistent hematopoietic mixed chimerism after bone marrow transplantation for thalassemia ma... by Marco Andreani, Manuela Testi, Javid Gaziev, Rossella Condello, Andrea Bontadini, Pier Luigi Tazzari, Francesca Ricci, Lidia De Felice, Francesca Agostini, Daniela Fraboni, Giuliana Ferrari, Mariarosa Battarra, Maria Troiano, Pietro Sodani, Guido Lucarelli
Published in Haematologica (2011-01-01)Get full text
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Plerixafor and G-CSF combination mobilizes hematopoietic stem and progenitors cells with a distinct transcriptional profile and a reduced in vivo homing capacity compared to plerix... by Maria Rosa Lidonnici, Annamaria Aprile, Marta Claudia Frittoli, Giacomo Mandelli, Ylenia Paleari, Antonello Spinelli, Bernhard Gentner, Matilde Zambelli, Cristina Parisi, Laura Bellio, Elena Cassinerio, Laura Zanaboni, Maria Domenica Cappellini, Fabio Ciceri, Sarah Marktel, Giuliana Ferrari
Published in Haematologica (2017-04-01)Get full text
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Imbalanced TGFβ signalling and autophagy drive erythroid priming of hematopoietic stem cells in β-thalassemia by Maria Rosa Lidonnici, Giulia Chianella, Nicole Mende, Hugo P. Bastos, Matteo Barcella, Ivan Merelli, Mariangela Storto, Valentina Romeo, Francesca Tiboni, Samantha Scaramuzza, Claudia Rossi, Laura Raggi, Annamaria Aprile, Stefania Crippa, Deena Iskander, Irene Roberts, Anastasios Karamiditris, Julia Keith, Christophe Lechauve, Mitchell J. Weiss, Nicola K. Wilson, Berthold Göttgens, Maria Ester Bernardo, Fabio Ciceri, Alessandro Aiuti, Sarah Marktel, Elisa Laurenti, Giuliana Ferrari
Published in Nature Communications (2025-07-01)Get full text
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