Search Results - Lujaina Elbakr
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Precise template-free correction restores gene function in Tay-Sachs disease while reframing is ineffective by Joshua E. Hung, Reid A. Brewer, Lujaina Elbakr, Antonio Mollica, Georgiana Forguson, Wing Suen Chan, Evgueni A. Ivakine
Published in Molecular Therapy: Nucleic Acids (2025-03-01)Get full text
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