Search Results - Maddison Knight
- Showing 1 - 5 results of 5
-
1
Characterization of the humanized FRG mouse model and development of an AAV-LK03 variant with improved liver lobular biodistribution by Marti Cabanes-Creus, Renina Gale Navarro, Sophia H.Y. Liao, Suzanne Scott, Rodrigo Carlessi, Ramon Roca-Pinilla, Maddison Knight, Grober Baltazar, Erhua Zhu, Matthew Jones, Elena Denisenko, Alistair R.R. Forrest, Ian E. Alexander, Janina E.E. Tirnitz-Parker, Leszek Lisowski
Published in Molecular Therapy: Methods & Clinical Development (2023-03-01)Get full text
Article -
2
AAV capsid bioengineering in primary human retina models by Adrian Westhaus, Steven S. Eamegdool, Milan Fernando, Paula Fuller-Carter, Alicia A. Brunet, Annie L. Miller, Rabab Rashwan, Maddison Knight, Maciej Daniszewski, Grace E. Lidgerwood, Alice Pébay, Alex Hewitt, Giorgia Santilli, Adrian J. Thrasher, Livia S. Carvalho, Anai Gonzalez-Cordero, Robyn V. Jamieson, Leszek Lisowski
Published in Scientific Reports (2023-12-01)Get full text
Article -
3
Impact of liver fibrosis on AAV-mediated gene transfer to mouse hepatocytes by Rosa Ferriero, Gemma Bruno, Agnese Padula, Simone Pisano, Iolanda Boffa, Marco Gargaro, Teresa Imperatore, Maria Battipaglia, Silvia Vivenzio, Claudia Perna, Edoardo Nusco, Luigi Ferrante, Adrian Westhaus, Maddison Knight, Giorgia Manni, Severo Campione, Evaristo Di Napoli, Elena Polishchuk, Roman Polishchuk, Orlando Paciello, Nicola Brunetti-Pierri, Leszek Lisowski, Francesca Fallarino, Pasquale Piccolo
Published in Nature Communications (2025-03-01)Get full text
Article -
4
Development of new adeno-associated virus capsid variants for targeted gene delivery to human cardiomyocytes by Cindy Y. Kok, Shinya Tsurusaki, Marti Cabanes-Creus, Sindhu Igoor, Renuka Rao, Rhys Skelton, Sophia H.Y. Liao, Samantha L. Ginn, Maddison Knight, Suzanne Scott, Mario Mietzsch, Rebecca Fitzsimmons, Jessica Miller, Tamer M.A. Mohamed, Robert McKenna, James J.H. Chong, Adam P. Hill, James E. Hudson, Ian E. Alexander, Leszek Lisowski, Eddy Kizana
Published in Molecular Therapy: Methods & Clinical Development (2023-09-01)Get full text
Article -
5
Harnessing whole human liver ex situ normothermic perfusion for preclinical AAV vector evaluation by Marti Cabanes-Creus, Sophia H. Y. Liao, Renina Gale Navarro, Maddison Knight, Deborah Nazareth, Ngee-Soon Lau, Mark Ly, Erhua Zhu, Ramon Roca-Pinilla, Ricardo Bugallo Delgado, Ana F. Vicente, Grober Baltazar, Adrian Westhaus, Jessica Merjane, Michael Crawford, Geoffrey W. McCaughan, Carmen Unzu, Gloria González-Aseguinolaza, Ian E. Alexander, Carlo Pulitano, Leszek Lisowski
Published in Nature Communications (2024-03-01)Get full text
Article
