Search Results - Maria Escolar
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O30: REKLAIM: A first in human phase Ib clinical trial of FBX-101 (AAVrh10.GALC) intravenously administered after UCBT for infantile Krabbe disease by Maria Escolar, Mark Vander Lugt, Raymond Wang, Juan Ruiz, Michele Poe, Paul Szabolcs
Published in Genetics in Medicine Open (2024-01-01)Get full text
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P014: First-in-human phase 1/2 trial of intravenous FBX-101 with cord blood transplantation increases GALC, brain and motor development in infantile Krabbe by Maria Escolar, Mark Vander Lugt, Michele Poe, Melissa Greco, Keith Werling, Erandi De Silva, Juan Ruiz, Paul Szabolcs
Published in Genetics in Medicine Open (2023-01-01)Get full text
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Population-Based Screening of Newborns: Findings From the NBS Expansion Study (Part One) by Amy Brower, Kee Chan, Marc Williams, Susan Berry, Robert Currier, Piero Rinaldo, Michele Caggana, Amy Gaviglio, William Wilcox, Robert Steiner, Ingrid A. Holm, Jennifer Taylor, Joseph J. Orsini, Luca Brunelli, Joanne Adelberg, Olaf Bodamer, Sarah Viall, Curt Scharfe, Melissa Wasserstein, Jin Y. Chen, Maria Escolar, Aaron Goldenberg, Kathryn Swoboda, Can Ficicioglu, Dieter Matern, Rachel Lee, Michael Watson
Published in Frontiers in Genetics (2022-07-01)Get full text
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