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Beyond Trikafta: new models to assess tissue dependent rescue of N1303K-CFTR by Iwona Pranke, Iwona Pranke, Valeria Capurro, Benoit Chevalier, Benoit Chevalier, Emanuela Pesce, Valeria Tomati, Cristina Pastorino, Mairead Kelly-Aubert, Mairead Kelly-Aubert, Aurelie Hatton, Aurelie Hatton, Elise Dreano, Elise Dreano, Mariateresa Lena, Mariateresa Lena, Renata Bocciardi, Renata Bocciardi, Federico Zara, Federico Zara, Stefano Pantano, Vito Terlizzi, Cristina Lucanto, Stefano Costa, Laura Claut, Valeria Daccò, Piercarlo Poli, Massimo Maschio, Benedetta Fabrizzi, Benedetta Fabrizzi, Nicole Caporelli, Nicole Caporelli, Marco Cipolli, Sonia Volpi, Frederique Chedevergne, Laure Cosson, Julie Macey, Sophie Ramel, Laurence Weiss, Dominique Grenet, Laurence Le Clainche-Viala, Benoit Douvry, Bruno Ravoninjatovo, Camille Audousset, Aurélie Tatopoulos, Bénédicte Richaud-Thiriez, Melissa Baravalle, Guillaume Thouvenin, Guillaume Labbé, Marie Mittaine, Philippe Reix, Isabelle Durieu, Julie Mankikian, Stéphanie Bui, Thao Nguyen-Khoa, Thao Nguyen-Khoa, Thao Nguyen-Khoa, Karim Khoukh, Clémence Martin, Clémence Martin, Clémence Martin, Jennifer Da Silva, Jennifer Da Silva, Paola De Carli, Carlo Castellani, Federico Cresta, Luis Galietta, Anne Guillemaut, Emmanuelle Girodon, Emmanuelle Girodon, Emmanuelle Girodon, Natacha Remus, Mathis Bulcaen, Marjolein Ensinck, Miroslaw Zajac, Marianne Carlon, Jean LeBihan, Pierre-Régis Burgel, Pierre-Régis Burgel, Pierre-Régis Burgel, Pierre-Régis Burgel, Isabelle Sermet-Gaudelus, Isabelle Sermet-Gaudelus, Isabelle Sermet-Gaudelus, Isabelle Sermet-Gaudelus, Alexandre Hinzpeter, Alexandre Hinzpeter, Nicoletta Pedemonte
Published in Frontiers in Pharmacology (2025-10-01)Get full text
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