Search Results - Michela Simbula
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Drugs Repurposing of Molecules Modulating Human Delta Globin Gene Expression via a Model of Transgenic Foetal Liver Cells: Implications for Beta-Hemoglobinopathy Therapeutics by Michela Simbula, Maria Francesca Manchinu, Stefania Olla, Michela Congiu, Simona Vaccargiu, Cristian Antonio Caria, Daniela Poddie, Maria Serafina Ristaldi
Published in Biomolecules (2025-04-01)Get full text
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In vivo activation of the human δ-globin gene: the therapeutic potential in β-thalassemic mice by Maria F. Manchinu, Maria F. Marongiu, Daniela Poddie, Carla Casu, Veronica Latini, Michela Simbula, Renzo Galanello, Paolo Moi, Antonio Cao, Susanna Porcu, Maria S. Ristaldi
Published in Haematologica (2014-01-01)Get full text
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miR-365-3p mediates BCL11A and SOX6 erythroid-specific coregulation: A new player in HbF activation by Michela Simbula, Maria Francesca Manchinu, Maura Mingoia, Mauro Pala, Isadora Asunis, Cristian Antonio Caria, Lucia Perseu, Manan Shah, Merlin Crossley, Paolo Moi, Maria Serafina Ristaldi
Published in Molecular Therapy: Nucleic Acids (2023-12-01)Get full text
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