Search Results - Michelle Lorentzos

  • Showing 1 - 3 results of 3
Refine Results
  1. 1

    Newborn screening for Duchenne muscular dystrophy: the perspectives of stakeholdersResearch in context by Charli Ji, Didu S. Kariyawasam, Hugo Sampaio, Michelle Lorentzos, Kristi J. Jones, Michelle A. Farrar

    Get full text
    Article


  2. 2

    Strategic consensus on the clinical translation of advanced therapies in paediatric rare neurological disorders by Natalie Y. Lim, Christian E. Meagher, Ann Bye, Michelle Lorentzos, Russell C. Dale, Shekeeb Mohammad, Katherine B. Howell, Elizabeth E. Palmer, Ian R. Woodcock, Emma Macdonald-Laurs, Anne Preisz, Nadia Badawi, Sandra T. Cooper, Stephen C. Hille, Toby N. Trahair, Anita Cairns, Nicholas Smith, Michelle A. Farrar, Didu S. Kariyawasam

    Published in Neurotherapeutics (2026-04-01)
    Get full text
    Article


  3. 3

    Confirmatory long-term efficacy and safety results of ataluren in patients with nmDMD from Study 041, an international, randomized, double-blind, placebo-controlled, Phase III tria... by Dmitry Vlodavets, Shiwen Wu, Anna Kostera-Pruszczyk, Jong-Hee Chae, Sheffali Gulati, Jin-Hong Shin, Michelle Lorentzos, Anita Cairns, Yuh-Jyh Jong, Hirofumi Komaki, Jeffrey Statland, Alexandra Prufer de Queiroz Campos Araujo, Juliana Gurgel-Giannetti, Yasuhiro Takeshima, Rosa E Escobar Cedillo, Peter Karachunski, Kazuhiro Haginoya, Vinay Penematsa, Connie Chou, Paula Williams, Christian Werner, Craig M McDonald

    Article


Search Tools: