檢索結果 - Nithya Selvan
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Preclinical efficacy and safety of AAVrh10-based plakophilin-2 gene therapy (LX2020) as a treatment for arrhythmogenic cardiomyopathy 由 Jing Zhang, Erika Joana Gutierrez-Lara, Aryanne Do, Lena Nguyen, Anju Nair, Nithya Selvan, Tim Fenn, Eric Adler, Richie Khanna, Farah Sheikh
發表在 npj Regenerative Medicine (2025-04-01)獲取全文
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Expression and processing of mature human frataxin after gene therapy in mice 由 Teerapat Rojsajjakul, Nithya Selvan, Bishnu De, Jonathan B. Rosenberg, Stephen M. Kaminsky, Dolan Sondhi, Peter Janki, Ronald G. Crystal, Clementina Mesaros, Richie Khanna, Ian A. Blair
發表在 Scientific Reports (2024-04-01)獲取全文
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