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TWELVE-MONTH INTERIM ANALYSIS OF EFFICACY AND SAFETY OF GIVOSIRAN, AN INVESTIGATIONAL RNAI THERAPEUTIC FOR ACUTE HEPATIC PORPHYRIA, IN THE ENVISION OPEN LABEL EXTENSION by R. Marchi, L. Duarte, S. E, B. M, R. Dc, S. P, S. U, A.P. P, B. Dm, E. Al, K. S, P. C, P. Jd
Published in Hematology, Transfusion and Cell Therapy (2020-11-01)Get full text
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