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TWELVE-MONTH INTERIM ANALYSIS OF EFFICACY AND SAFETY OF GIVOSIRAN, AN INVESTIGATIONAL RNAI THERAPEUTIC FOR ACUTE HEPATIC PORPHYRIA, IN THE ENVISION OPEN LABEL EXTENSION 著者: R. Marchi, L. Duarte, S. E, B. M, R. Dc, S. P, S. U, A.P. P, B. Dm, E. Al, K. S, P. C, P. Jd
出版年 Hematology, Transfusion and Cell Therapy (2020-11-01)全文の入手
論文
