Search Results - Rachel M. Bailey

  • Showing 1 - 5 results of 5
Refine Results
  1. 1

    Toward a translational gene therapy for mucolipidosis IV by Brina Snyder, Rachel M. Bailey

    Get full text
    Article


  2. 2

    Editorial: Personalized medicine for neuromuscular disorders by Marc Bartoli, Rachel M. Bailey, Rachel M. Bailey, Kathrin Meyer, Kathrin Meyer, Florian Barthélémy, Florian Barthélémy

    Get full text
    Article


  3. 3

    Gene Therapy: Novel Approaches to Targeting Monogenic Epilepsies by Kimberly Goodspeed, Rachel M. Bailey, Rachel M. Bailey, Suyash Prasad, Chanchal Sadhu, Jessica A. Cardenas, Mary Holmay, Deborah A. Bilder, Berge A. Minassian

    Published in Frontiers in Neurology (2022-06-01)
    Get full text
    Article


  4. 4

    Advancing the pathologic phenotype of giant axonal neuropathy: early involvement of the ocular lens by Diane Armao, Thomas W. Bouldin, Rachel M. Bailey, Jody E. Hooper, Diana X. Bharucha, Steven J. Gray

    Published in Orphanet Journal of Rare Diseases (2019-02-01)
    Get full text
    Article


  5. 5

    Preclinical use of a clinically-relevant scAAV9/SUMF1 vector for the treatment of multiple sulfatase deficiency by Maximiliano Presa, Rachel M. Bailey, Somdatta Ray, Lauren Bailey, Saurabh Tata, Tara Murphy, Pierre-Alexandre Piec, Harold Combs, Steven J. Gray, Cathleen Lutz

    Published in Communications Medicine (2025-01-01)
    Get full text
    Article


Search Tools: