検索結果 - Ramon Díaz-Trelles
- 検索結果 1 - 3 結果 / 3
-
1
Development of an mRNA replacement therapy for phenylketonuria 著者: Carlos G. Perez-Garcia, Ramon Diaz-Trelles, Jerel Boyd Vega, Yanjie Bao, Marciano Sablad, Patty Limphong, Simon Chikamatsu, Hailong Yu, Wendy Taylor, Priya P. Karmali, Kiyoshi Tachikawa, Padmanabh Chivukula
出版年 Molecular Therapy: Nucleic Acids (2022-06-01)全文の入手
論文 -
2
Lipid nanoparticle delivers phenylalanine ammonia lyase mRNA to the liver leading to catabolism and clearance of phenylalanine in a phenylketonuria mouse model 著者: Ramon Diaz-Trelles, Sharon Lee, Kristen Kuakini, Jenny Park, Adrian Dukanovic, Jose A. Gonzalez, Thanhchau Dam, Jae Heon Kim, Jerel Boyd Vega, Marciano Sablad, Priya P. Karmali, Kiyoshi Tachikawa, Padmanabh Chivukula
出版年 Molecular Genetics and Metabolism Reports (2022-09-01)全文の入手
論文 -
3
Downregulation of hepatic lipopolysaccharide binding protein improves lipogenesis-induced liver lipid accumulation 著者: Jessica Latorre, Ramon Díaz-Trelles, Ferran Comas, Aleix Gavaldà-Navarro, Edward Milbank, Nathalia Dragano, Samantha Morón-Ros, Rajesh Mukthavaram, Francisco Ortega, Anna Castells-Nobau, Núria Oliveras-Cañellas, Wifredo Ricart, Priya P. Karmali, Kiyoshi Tachikawa, Pad Chivukula, Francesc Villarroya, Miguel López, Marta Giralt, José Manuel Fernández-Real, José María Moreno-Navarrete
出版年 Molecular Therapy: Nucleic Acids (2022-09-01)全文の入手
論文
