検索結果 - Raul Chertkoff
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Exploring delayed diagnosis in Gaucher disease: insights from a community survey and potential solutions 著者: Diana Paulina Peña Aragón, Tanya Collin-Histed, Magy Abdelwahab, Jesús Villarrubia Espinosa, Raul Chertkoff, Andre Balzekiene, Jessica Pacey
出版年 Orphanet Journal of Rare Diseases (2026-02-01)全文の入手
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Safety and efficacy of pegunigalsidase alfa in patients with Fabry disease who were previously treated with agalsidase alfa: results from BRIDGE, a phase 3 open-label study 著者: Aleš Linhart, Gabriela Dostálová, Kathy Nicholls, Michael L. West, Camilla Tøndel, Ana Jovanovic, Pilar Giraldo, Bojan Vujkovac, Tarekegn Geberhiwot, Einat Brill-Almon, Sari Alon, Raul Chertkoff, Rossana Rocco, Derralynn Hughes
出版年 Orphanet Journal of Rare Diseases (2023-10-01)全文の入手
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3
P006: Long-term safety and efficacy of pegunigalsidase alfa administered every 4 weeks in Fabry disease: 2-Year interim results from BRIGHT51 著者: John Bernat, Myrl Holida, Nicola Longo, Ozlem Goker-Alpan, Eric Wallace, Patrick Deegan, Camilla Tondel, Francois Eyskens, Ulla Feldt-Rasmussen, Derralynn Hughes, Antonio Pisani, Ales Linhart, Rossana Rocco, Einat Almon, Sari Alon, Raul Chertkoff, David Warnock, Stephen Waldek, William Wilcox
出版年 Genetics in Medicine Open (2023-01-01)全文の入手
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Long-term efficacy and safety of pegunigalsidase alfa administered every 4 weeks in adults with Fabry disease: results from up to 5 years of the BRIGHT F51 phase III, open-label ex... 著者: Myrl Holida, Aleš Linhart, Nicola Longo, Eric Wallace, Camilla Tøndel, Derralynn Hughes, David G. Warnock, Antonio Pisani, François Eyskens, Patrick Deegan, Ulla Feldt-Rasmussen, Ozlem Goker-Alpan, Ankit Mehta, Giovanni Piotti, Vito Fichera, Meng Wang, Raul Chertkoff, Stephen Waldek, William R. Wilcox, John A. Bernat
出版年 Orphanet Journal of Rare Diseases (2026-03-01)全文の入手
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P236: Extending the interval between pegunigalsidase alfa infusions in patients with Fabry disease: Five-year interim results from the ongoing BRIGHT51 study 著者: John Bernat, Myrl Holida, Stephen Waldek, William Wilcox, Nicola Longo, Ozlem Goker-Alpan, Eric Wallace, Patrick Deegan, Camilla Tondel, François Eyskens, Ulla Feldt-Rasmussen, Derralynn Hughes, Antonio Pisani, Ankit Mehta, Khan Nedd, David Warnock, Giovanni Piotti, Meng Wang, Einat Almon-Brill, Sari Alon, Raul Chertkoff, Ales Linhart
出版年 Genetics in Medicine Open (2025-01-01)全文の入手
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P005: Head-to-head trial of pegunigalsidase alfa vs agalsidase beta in Fabry disease: Phase 3 randomized, double-blind, BALANCE Study 2-year results 著者: John Bernat, Eric Wallace, Ozlem Goker-Alpan, William Wilcox, Myrl Holida, Nicola Longo, Derralynn Hughes, Pilar Giraldo, Maria Molnar, Damara Ortiz, Robert Hopkin, Camilla Tondel, Ales Linhart, Patrick Deegan, Ana Jovanovic, Michael Muriello, Bruce Barshop, Virginia Kimonis, Bojan Vujkovac, Albina Nowak, Tarekegn Hiwot, Antonio Pisani, Dominique Germain, Ilkka Kantola, Jasmine Knoll, Ankit Mehta, Stephen Waldek, Einat Almon, Sari Alon, Raul Chertkoff, Rossana Rocco, David Warnock
出版年 Genetics in Medicine Open (2023-01-01)全文の入手
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