Search Results - S W-Pipe

Guidelines for management of hemophilia—why, what, and how? by Alok Srivastava, Johnny Mahlangu, Steven W. Pipe

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Efficacy of emicizumab in a pediatric patient with type 3 von Willebrand disease and alloantibodies by Angela C. Weyand, Veronica H. Flood, Jordan A. Shavit, Steven W. Pipe

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SAFETY AND EFFICACY OF THE FITUSIRAN REVISED ANTITHROMBIN-BASED DOSE REGIMEN IN PEOPLE WITH HAEMOPHILIA A OR B, WITH OR WITHOUT INHIBITORS (ATLAS-OLE) by Guy-Young, Kaan-Kavakli, S W-Pipe, Alok-Srivastava, Juliana-Aragao, L A-Menapace, Chuanwu-Zhang, Marja-Puurunen, Marek-Demissie, Gili-Kenet

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Hemophilia gene therapy knowledge and perceptions: Results of an international survey by Flora Peyvandi, David Lillicrap, Johnny Mahlangu, Claire McLintock, K. John Pasi, Steven W. Pipe, Wendy Scales, Alok Srivastava, Thierry VandenDriessche

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SURGICAL EXPERIENCE IN PEOPLE WITH HEMOPHILIA A OR B WITH AND WITHOUT INHIBITORS RECEIVING FITUSIRAN by Alok-Srivastava, Pencho-Georgiev, Toshko-Lissitchkov, M V-Ragni, Juliana-Aragao, L A-Menapace, Yuqian-Shen, Marja-Puurunen, Marek-Demissie, S W-Pipe

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Recombinant factor VIIa: new insights into the mechanism of action through product innovation by Miguel A. Escobar, Maureane Hoffman, Giancarlo Castaman, Cedric Hermans, Johnny Mahlangu, Johannes Oldenburg, Charles L. Percy, Mark T. Reding, Amy D. Shapiro, Steven W. Pipe

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GLOBAL COMPARATIVE ANTITHROMBIN-FIELD STUDY: IMPACT OF LABORATORY ASSAY VARIABILITY ON THE ASSESSMENT OF ANTITHROMBIN ACTIVITY MEASUREMENT by E Seth-Chhabra, A Sadeghi-Khomami, Mingjie-Liu, Guy-Young, S W-Pipe, MC Ozelo, C Le-Camus, M Toh, SA Lima-Montalvao, Marek-Demissie

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Activated prothrombin complex concentrate in patients receiving emicizumab prophylaxis: from evidence to clinical practice by Robert F. Sidonio, Jr., Guy Young, Carmen Escuriola Ettingshausen, Johnny Mahlangu, Margareth C. Ozelo, Alok Srivastava, Jerzy Windyga, Hye–Youn Lee, Aurelia Lelli, Steven W. Pipe

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Outcomes and management of invasive procedures in participants with hemophilia A post gene therapy: a post hoc analysis of the GENEr8-1 phase III trial by Doris V. Quon, Jiaan-Der Wang, Michael Wang, Dominic Pepperell, Young-Shil Park, Gili Kenet, Johnny Mahlangu, Teh-Liane Khoo, Tara M. Robinson, Konstantia-Maria Chavele, Steven W. Pipe

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Etranacogene dezaparvovec (AMT-061 phase 2b): normal/near normal FIX activity and bleed cessation in hemophilia B by Annette Von Drygalski, Adam Giermasz, Giancarlo Castaman, Nigel S. Key, Susan Lattimore, Frank W.G. Leebeek, Wolfgang Miesbach, Michael Recht, Alison Long, Robert Gut, Eileen K. Sawyer, Steven W. Pipe

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Natural history of preexisting AAV5 antibodies in adults with hemophilia B during the lead-in of the etranacogene dezaparvovec phase 3 study by Robert Klamroth, Michael Recht, Nigel S. Key, Wolfgang Miesbach, Steven W. Pipe, Radoslaw Kaczmarek, Douglass Drelich, Blanca Salazar, Sandra Le Quellec, Paul E. Monahan, Nicholas Galante, Paul van der Valk, Jacqueline Tarrant

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Long-term safety and efficacy of fitusiran prophylaxis, and perioperative management, in people with hemophilia A or B by Steven W. Pipe, Toshko Lissitchkov, Pencho Georgiev, Sarah Mangles, Inga Hegemann, Alice Trinchero, Pratima Chowdary, Adam Forbes, Liqi Feng, Laurel A. Menapace, Salim Kichou, Shauna Andersson, Marek Demissie, Margaret V. Ragni

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Completion of phase 2b trial of etranacogene dezaparvovec gene therapy in patients with hemophilia B over 5 years by Annette von Drygalski, Esteban Gomez, Adam Giermasz, Giancarlo Castaman, Nigel S. Key, Susan U. Lattimore, Frank W. G. Leebeek, Wolfgang A. Miesbach, Michael Recht, Paul E. Monahan, Sandra Le Quellec, Steven W. Pipe

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Adeno-associated virus-based gene therapy for hemophilia–addressing the gaps by Wolfgang Miesbach, Paul Batty, Pratima Chowdary, Sylvia Fong, Radoslaw Kaczmarek, Frank W.G. Leebeek, Brian Long, Johnny Mahlangu, Mike Makris, Glenn F. Pierce, Steven W. Pipe, Alok Srivastava, Jan Voorberg, Flora Peyvandi

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Treatment of severe bleeds with eptacog beta in hemophilia A or B with inhibitors: a post hoc analysis of the PERSEPT 1 and 2 trials by Guy Young, Johnny Mahlangu, Lisa N. Boggio, Manuel Carcao, Yesim Dargaud, Miguel Escobar, Adam Giermasz, Cédric Hermans, Philip Kuriakose, Wolfgang Miesbach, Danielle Nance, Amina Rafique, Robert F. Sidonio, Jr., Kateryna V. Vilchevska, Michael Wang, Steven W. Pipe

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Development of a novel gene editing lexicon for hemophilia: methodology and results by Craig M. Kessler, Leonard A. Valentino, Courtney D. Thornburg, Carmen Unzu, Mark A. Kay, Flora Peyvandi, Penni Smith, Wolfgang Miesbach, William McKeown, Glenn F. Pierce, Kate Khair, Katarina Starcevic, Monisha Pillai, Micheala Jones, Anil Sindhurakar, Lauren Whyte, Virginie Delwart, Megan Chiao, David E. Gutstein, Ilia Antonino, Cedric Hermans, Steven W. Pipe

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Efficacy, safety, and quality of life 4 years after valoctocogene roxaparvovec gene transfer for severe hemophilia A in the phase 3 GENEr8-1 trial by Andrew D. Leavitt, Johnny Mahlangu, Priyanka Raheja, Emily Symington, Doris V. Quon, Adam Giermasz, Maria Fernanda López Fernández, Gili Kenet, Gillian Lowe, Nigel S. Key, Carolyn M. Millar, Steven W. Pipe, Bella Madan, Sheng-Chieh Chou, Robert Klamroth, Jane Mason, Hervé Chambost, Flora Peyvandi, Elaine Majerus, Dominic Pepperell, Christine Rivat, Hua Yu, Tara M. Robinson, Margareth C. Ozelo

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