Search Results - Tyra Estwick
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A First-in-Human Base Edit Gene Therapy for CD40L Deficiency X-Linked Hyper IgM (XHIGM) Syndrome by Suk See De Ravin, Tyra Estwick, Yuzhi Yin, Michelle Ma, Siyuan Liu, Xiaolin Wu, Justin Lack, Andres Zea Vera, Colin Sweeney, Stephen L. Highfill, Christian Wysocki, Ronald J. Meis, Gary A. Dahl, Benjamin P. Kleinstiver, Harry L. Malech
Published in Journal of Human Immunity (2026-05-01)Get full text
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Lentivector cryptic splicing mediates increase in CD34+ clones expressing truncated HMGA2 in human X-linked severe combined immunodeficiency by Suk See De Ravin, Siyuan Liu, Colin L. Sweeney, Julie Brault, Narda Whiting-Theobald, Michelle Ma, Taylor Liu, Uimook Choi, Janet Lee, Sandra Anaya O’Brien, Priscilla Quackenbush, Tyra Estwick, Anita Karra, Ethan Docking, Nana Kwatemaa, Shuang Guo, Ling Su, Zhonghe Sun, Sheng Zhou, Jennifer Puck, Morton J. Cowan, Luigi D. Notarangelo, Elizabeth Kang, Harry L. Malech, Xiaolin Wu
Published in Nature Communications (2022-06-01)Get full text
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