Consensus on Complement Inhibitor Therapy and Management of Paroxysmal Nocturnal Hemoglobinuria

Paroxysmal nocturnal hemoglobinuria (PNH), a rare clonal disease of hematopoietic stem cells caused by mutations in the phosphatidylinositol N-acetylglucosaminyltransferase subunit A (PIGA) gene, may lead to the deficiency of glycosylated phosphatidylinositol (GPI)-anchored proteins. This deficiency...

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التفاصيل البيبلوغرافية

الحاوية / القاعدة:	罕见病研究
المؤلف الرئيسي:	Red Blood Cell Disease (Anemia) Group, Chinese Society of Hematology, Chinese Medical Association
التنسيق:	مقال
اللغة:	الصينية
منشور في:	Editorial Office of Journal of Rare Diseases 2025-01-01
الموضوعات:	paroxysmal nocturnal hemoglobinuria intravascular hemolysis extravascular hemolysis proximal complement inhibitors terminal complement inhibitors consensus
الوصول للمادة أونلاين:	https://jrd.chard.org.cn/article/doi/10.12376/j.issn.2097-0501.2025.01.012