P261: Vestronidase alfa for the treatment of mucopolysaccharidosis VII (MPS VII): Updated results from a longitudinal, multicenter disease monitoring program (DMP)

Bibliographic Details
Published in:Genetics in Medicine Open
Main Authors: Roberto Giugliani, Antonio Gonzalez-Meneses, Christina Grant, Maurizio Scarpa, Angela Sun, Raymond Wang, Barbara Burton, Ans van der Ploeg, Esmeralda Martins, Consuelo Durand, Brigitte Chabrol, Joel Hetzer, Deborah Marsden, J. Lawrence Merritt, II
Format: Article
Language:English
Published: Elsevier 2024-01-01
Online Access:http://www.sciencedirect.com/science/article/pii/S2949774424003030
Description
ISSN:2949-7744

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