Restoration of brain dystrophin using tricyclo-DNA ASOs restores neurobehavioral deficits in DMD mice
| Published in: | Molecular Therapy: Nucleic Acids |
|---|---|
| Main Authors: | Muthukumar Karuppasamy, Matthew S. Alexander |
| Format: | Article |
| Language: | English |
| Published: |
Elsevier
2023-06-01
|
| Online Access: | http://www.sciencedirect.com/science/article/pii/S2162253123000938 |
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