Development of orphan drugs for rare diseases
Most rare diseases (orphan diseases) still lack approved treatment options despite major advances in research providing the necessary tools to understand their molecular basis and legislation providing regulatory and economic incentives to expedite the development of specific therapies. Addressing t...
| Published in: | Clinical and Experimental Pediatrics |
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| Main Author: | |
| Format: | Article |
| Language: | English |
| Published: |
The Korean Pediatric Society
2024-07-01
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| Subjects: | |
| Online Access: | http://www.e-cep.org/upload/pdf/cep-2023-00535.pdf |