P1424: ONE-YEAR FOLLOW-UP OF A PHASE 2 STUDY OF MITAPIVAT, AN ORAL PYRUVATE KINASE ACTIVATOR, FOR THE TREATMENT OF SICKLE CELL DISEASE

Bibliographic Details
Published in:HemaSphere
Main Authors: Myrthe van Dijk, Minke Rab, Brigitte van Oirschot, Jennifer Bos, Cleo Derichs, Anita Rijneveld, Marjon Cnossen, Erfan Nur, Bart Biemond, Marije Bartels, Judith Jans, Wouter van Solinge, Roger Schutgens, Richard Van Wijk, Eduard van Beers
Format: Article
Language:English
Published: Wiley 2023-08-01
Online Access:http://journals.lww.com/10.1097/01.HS9.0000972584.29706.31