Hematopoietic stem cell transplantation in pediatric patients with type VI mucopolysaccharidosis

Background It is uncertain whether hematopoietic stem cell transplantation (HSCT), versus standard enzyme replacement therapy (ERT), is effective for type VI mucopolysaccharidosis (MPS VI). Purpose New related advances in HSCT prompted an examination of the transplant procedures performed in a recen...

Full description

Bibliographic Details

Published in:	Clinical and Experimental Pediatrics
Main Authors:	Vedat Uygun, Koray Yalçın, Hayriye Daloğlu, Seda Öztürkmen, Suna Çelen, Suleimen Zhumatayev, Gülsün Karasu, Akif Yeşilipek
Format:	Article
Language:	English
Published:	The Korean Pediatric Society 2025-08-01
Subjects:	mucopolysaccharidoses hematopoietic stem cell transplantation enzyme replacement therapy child maroteaux-lamy syndrome
Online Access:	http://www.e-cep.org/upload/pdf/cep-2024-02033.pdf