State of the Art on Approved Cystic Fibrosis Transmembrane Conductance Regulator (<i>CFTR</i>) Modulators and Triple-Combination Therapy

Cystic fibrosis (CF) is the most common life-limiting inherited disease in Caucasian populations, affecting approximately 80,000 people worldwide. CF is a complex multi-organ monogenic autosomal recessive disorder caused by a mutation in cystic fibrosis transmembrane conductance regulator (<i>...

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發表在:	Pharmaceuticals
Main Authors:	Aniello Meoli, Valentina Fainardi, Michela Deolmi, Giulia Chiopris, Francesca Marinelli, Caterina Caminiti, Susanna Esposito, Giovanna Pisi
格式:	Article
語言:	英语
出版:	MDPI AG 2021-09-01
主題:	<i>CFTR</i> <i>CFTR</i> modulator cystic fibrosis F508del ivacaftor
在線閱讀:	https://www.mdpi.com/1424-8247/14/9/928