DP096 | COMBINATION OF 5-AZACITIDINE AND RUXOLITINIB IN VEXAS SYNDROME: A RETROSPECTIVE STUDY

Introduction: VEXAS (Vacuoles, E1 enzyme, X-linked, Autoinflammatory, Somatic) syndrome is an autoinflammatory condition caused by somatic UBA1 mutations in hematopoietic progenitors, frequently associated with cytopenias and myelodysplastic syndromes (MDS) in ~50% of cases. No standardized therapy...

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Bibliographic Details

Published in:	Haematologica
Main Authors:	G.M. Bergonzi, E. Cozzo, A. Tomelleri, C. Piccolo, G. Scorpio, L. Vago, F. Ciceri, L. Dagna, C. Campochiaro, E. Diral
Format:	Article
Language:	English
Published:	Ferrata Storti Foundation 2025-09-01
Online Access:	https://haematologica.org/article/view/12563