Stages of research and development of therapeutic approaches for Duchenne myodystrophy. Part I: the period before etiotropic approaches introduction
Duchenne muscular dystrophy is one of the most common inherited muscular dystrophies. The cause of this disease with an X‑linked recessive type of inheritance is mutations of the DMD gene, leading to the absence of the dystrophin protein this gene encodes or its impaired function. Loss of dystrophin...
| Published in: | Нервно-мышечные болезни |
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| Main Authors: | , , |
| Format: | Article |
| Language: | Russian |
| Published: |
ABV-press
2024-03-01
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| Subjects: | |
| Online Access: | https://nmb.abvpress.ru/jour/article/view/590 |