P028: Switching treatment to cipaglucosidase alfa+miglustat positively affects motor function and quality of life in patients with late-onset Pompe disease

書誌詳細
出版年:Genetics in Medicine Open
主要な著者: Priya Kishnani, Barry Byrne, Kristl Claeys, Paula Clemens, Jordi Díaz-Manera, Mazen Dimachkie, Hani Kushlaf, Tahseen Mozaffar, Mark Roberts, Antonio Toscano, Noemi Hummel, Fred Holdbrook, Simon Shohet, Benedikt Schoser
フォーマット: 論文
言語:英語
出版事項: Elsevier 2024-01-01
オンライン・アクセス:http://www.sciencedirect.com/science/article/pii/S2949774424000517