GENETIC AND NON-GENETIC DETERMINANTS OF SUCCESSFUL IMMUNE TOLERANCE INDUCTION IN PEOPLE WITH SEVERE HEMOPHILIA A

Background: Eradicating inhibitors to restore the effectiveness of Factor VIII (FVIII) is a desirable treatment goal for People with Severe Hemophilia A (PwSHA) and inhibitors, as this enables treatment of bleeding episodes with FVIII concentrates. However, since Immune Tolerance Induction (ITI) is...

وصف كامل

التفاصيل البيبلوغرافية
الحاوية / القاعدة:Hematology, Transfusion and Cell Therapy
المؤلفون الرئيسيون: I Oomen, RM Camelo, M Carcao, G Castaman, JCJ Eikenboom, K Fischer, WG Frank Leebeek, D Lillicrap, ME Mancuso, D Matino, DMN Di Minno, AB Mohseny, J Oldenburg, SM Rezende, GE Rivard, N Rydz, S Schols, Voorberg Jan, FMRA Callado, LEM Carvalho, VKB Franco, CS Lorenzato, K Fijnvandraat, S Gouw
التنسيق: مقال
اللغة:الإنجليزية
منشور في: Elsevier 2024-10-01
الوصول للمادة أونلاين:http://www.sciencedirect.com/science/article/pii/S253113792401277X