Ocular development after highly effective modulator treatment early in life

Highly effective cystic fibrosis (CF) transmembrane conductance regulator (CFTR) modulator therapies (HEMT), including elexacaftor-tezacaftor-ivacaftor, correct the underlying molecular defect causing CF. HEMT decreases general symptom burden by improving clinical metrics and quality of life for mos...

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書目詳細資料
發表在:Frontiers in Pharmacology
Main Authors: Yimin Zhu, Danni Li, Felisa Reyes-Ortega, Holly R. Chinnery, Elena K. Schneider-Futschik
格式: Article
語言:英语
出版: Frontiers Media S.A. 2023-09-01
主題:
在線閱讀:https://www.frontiersin.org/articles/10.3389/fphar.2023.1265138/full