Analysis of the efficacy and adverse effects of nusinersen in the treatment of children with spinal muscular atrophy in China

Abstract Objective This study was based on a retrospective clinical observational cohort study of a two‐center application of nusinersen in China to evaluate the clinical efficacy and adverse effects of nusinersen in the treatment of SMA (spinal muscular atrophy) Types 1–3. Methods Clinical data fro...

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Bibliographic Details
Published in:Brain and Behavior
Main Authors: Dan Li, Jie Yang, Xueying Wang, Lin Yang, Rong Luo, Shaoping Huang
Format: Article
Language:English
Published: Wiley 2024-07-01
Subjects:
Online Access:https://doi.org/10.1002/brb3.3630