Emicizumab in children: bleeding episodes and outcome before and after transition to Emicizumab

Abstract Purpose Real-world data and study data regarding therapy with Emicizumab in pediatric cohorts with haemophilia A is scarce. Especially, data on previously untreated pediatric patients (PUPs) and minimally treated patients (MTPs) are missing. Methods Thirteen pediatric patients with haemophi...

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發表在:	BMC Pediatrics
Main Authors:	Hannah Glonnegger, Felicia Andresen, Friedrich Kapp, Stefano Malvestiti, Martin Büchsel, Barbara Zieger
格式:	Article
語言:	英语
出版:	BMC 2022-08-01
主題:	Emicizumab Hemlibra Children Annual bleeding rate
在線閱讀:	https://doi.org/10.1186/s12887-022-03546-1