Haploidentical stem cell transplantation with posttransplant cyclophosphamide in children with Wiskott–Aldrich syndrome: a case report

Wiskott–Aldrich syndrome (WAS) is a condition characterized by a low platelet count, eczema, and a weakened immune system. Hematopoietic stem cell transplantation (HSCT) is the only curative treatment option. Haploidentical HSCT with posttransplant cyclophosphamide (PTCy) is an emerging approach for...

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Bibliographic Details

Published in:	Frontiers in Immunology
Main Authors:	Le Nguyen Ngoc Quynh, Binh Nguyen Thanh, Lien Luong Thi, Thuy Nguyen Thi Dieu, Duong Dang Anh, Pamela P. Lee, Tung Cao Viet, Dien Tran Minh
Format:	Article
Language:	English
Published:	Frontiers Media S.A. 2025-02-01
Subjects:	Wiskott–Aldrich syndrome thrombocytopenia inborn error immunity hematopoietic stem cell transplantation posttransplant cyclophosphamide
Online Access:	https://www.frontiersin.org/articles/10.3389/fimmu.2025.1495666/full