Generation of three Duchenne Muscular Dystrophy patient-specific induced pluripotent stem cell lines DMD_YoTaz_PhyMedEXp, DMD_RaPer_PhyMedEXp, DMD_OuMen_PhyMedEXp (INSRMi008-A, INSRMi009-A and INSRMi010-A)

Duchenne Muscular Dystrophy (DMD) is a X-linked degenerative pathology with a prevalence of 1/3600–6000 boys due to the absence of functional dystrophin in muscles. This muscular disease leads to skeletal muscle damages, respiratory failure and in the later stages dilated cardiomyopathy (DCM) leadin...

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Bibliographic Details
Published in:Stem Cell Research
Main Authors: Monia Souidi, Pascal Amédro, Pierre Meyer, Romain Desprat, Jean-Marc Lemaître, François Rivier, Alain Lacampagne, Albano C. Meli
Format: Article
Language:English
Published: Elsevier 2020-12-01
Online Access:http://www.sciencedirect.com/science/article/pii/S1873506120303950