Recent Advances in Gene Therapy for Hemophilia
Hemophilia, an X-linked monogenic disorder, arises from mutations in the F8 or F9 genes, which encode clotting factor VIII (FVIII) or clotting factor IX (FIX), respectively. As a prominent hereditary coagulation disorder, hemophilia is clinically manifested by spontaneous hemorrhagic episodes. Sever...
| Published in: | Clinical and Applied Thrombosis/Hemostasis |
|---|---|
| Main Authors: | , , , , , , , , |
| Format: | Article |
| Language: | English |
| Published: |
SAGE Publishing
2025-09-01
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| Online Access: | https://doi.org/10.1177/10760296251378455 |