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P314: Long-term safety and sustained functional benefit in patients with DMD 4 years post-treatment with delandistrogene moxeparvovec: A phase 1/2a study*

Bibliographic Details
Published in:Genetics in Medicine Open
Main Authors: Erin O’Rourke, Jerry R. Mendell, Zarife Sahenk, Kelly J. Lehman, Linda P. Lowes, Natalie F. Reash, Megan Iammarino, Lindsay Alfano, Sarah Lewis, Kathleen Church, Richard Shell, Rachael A. Potter, Danielle Griffin, Mark J. Hogan, Shufang Wang, Stefanie Mason, Eddie Darton, Louise Rodino-Klapac
Format: Article
Language:English
Published: Elsevier 2023-01-01
Online Access:http://www.sciencedirect.com/science/article/pii/S2949774423003424
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http://www.sciencedirect.com/science/article/pii/S2949774423003424

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