Genome Editing as a Treatment for the Most Prevalent Causative Genes of Autosomal Dominant Retinitis Pigmentosa
Inherited retinal dystrophies (IRDs) are a clinically and genetically heterogeneous group of diseases with more than 250 causative genes. The most common form is retinitis pigmentosa. IRDs lead to vision impairment for which there is no universal cure. Encouragingly, a first gene supplementation the...
Main Authors: | Michalitsa Diakatou, Gaël Manes, Beatrice Bocquet, Isabelle Meunier, Vasiliki Kalatzis |
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Format: | Article |
Language: | English |
Published: |
MDPI AG
2019-05-01
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Series: | International Journal of Molecular Sciences |
Subjects: | |
Online Access: | https://www.mdpi.com/1422-0067/20/10/2542 |
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