Population pharmacokinetics and pharmacodynamics of cysteamine in nephropathic cystinosis patients

Population pharmacokinetics and pharmacodynamics of cysteamine in nephropathic cystinosis patients

<p>Abstract</p> <p>Background</p> <p>Nephropathic cystinosis is an autosomal recessive disorder resulting in an impaired transport of cystine trough the lysosomal membrane causing an accumulation of free cystine in lysosomes. The only specific treatment for nephropathic...

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Bibliographic Details
Main Authors: Bouazza Naïm, Tréluyer Jean-Marc, Ottolenghi Chris, Urien Saik, Deschenes Georges, Ricquier Daniel, Niaudet Patrick, Chadefaux-Vekemans Bernadette
Format: Article
Language:English
Published: BMC 2011-12-01
Series:Orphanet Journal of Rare Diseases
Subjects:
population pharmacokinetics
pharmacodynamics
cysteamine
cystinosis
Online Access:http://www.ojrd.com/content/6/1/86

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