The Use of Tricyclo-DNA Oligomers for the Treatment of Genetic Disorders
Antisense Oligonucleotides (ASOs) represent very attractive therapeutic compounds for the treatment of numerous diseases. The antisense field has remarkably progressed over the last few years with the approval of the first antisense drugs and with promising developments of more potent and nuclease r...
Main Authors: | Philippine Aupy, Lucía Echevarría, Karima Relizani, Aurélie Goyenvalle |
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Format: | Article |
Language: | English |
Published: |
MDPI AG
2017-12-01
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Series: | Biomedicines |
Subjects: | |
Online Access: | https://www.mdpi.com/2227-9059/6/1/2 |
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