How to Value Orphan Drugs? A Review of European Value Assessment Frameworks

How to Value Orphan Drugs? A Review of European Value Assessment Frameworks

Background: Decision-makers have implemented a variety of value assessment frameworks (VAFs) for orphan drugs in European jurisdictions, which has contributed to variations in access for rare disease patients. This review provides an overview of the strengths and limitations of VAFs for the reimburs...

Full description

Bibliographic Details
Main Authors:	Alessandra Blonda, Yvonne Denier, Isabelle Huys, Steven Simoens
Format:	Article
Language:	English
Published:	Frontiers Media S.A. 2021-05-01
Series:	Frontiers in Pharmacology
Subjects:	orphan drug rare disease value assessment framework multi-criteria decision analysis (MCDA) decision-making economic evaluation
Online Access:	https://www.frontiersin.org/articles/10.3389/fphar.2021.631527/full

Similar Items

Implementing reflective multicriteria decision analysis (MCDA) to assess orphan drugs value in the Catalan Health Service (CatSalut)
by: Laura Guarga, et al.
Published: (2019-06-01)

Multi-criteria decision analysis for assessment and appraisal of orphan drugs
by: Georgi Iskrov, et al.
Published: (2016-09-01)

Multi-Criteria Decision Analysis (MCDA) Models in Health Technology Assessment of Orphan Drugs—a Systematic Literature Review. Next Steps in Methodology Development?
by: Aleksandra Baran-Kooiker, et al.
Published: (2018-10-01)

APPLICATION OF MULTIPLE-CRITERIA ANALYSIS FOR OPTIMIZATION OF FINANCING OF RARE DISEASES
by: V. V. Omelyanovskiy, et al.
Published: (2015-05-01)

Measuring trade-offs among criteria in a balanced scorecard framework: possible contributions from the multiple criteria decision analysis research field
by: Fernando A. F. Ferreira
Published: (2013-06-01)

Anxiety, Depression, Stress, and Decision-Making Among Orphans and Non-Orphans in Pakistan
by: Shafiq F, et al.
Published: (2020-03-01)

Impact on decision making framework for medicine purchasing in Chinese public hospital decision-making: determining the value of five dipeptidyl peptidase 4 (DPP-4) inhibitors
by: Yun Bao, et al.
Published: (2021-08-01)

Revealed preferences towards the appraisal of orphan drugs in Poland - multi criteria decision analysis
by: Katarzyna Kolasa, et al.
Published: (2018-04-01)

Determining the value contribution of selexipag for the treatment of pulmonary arterial hypertension (PAH) in Spain using reflective multi-criteria decision analysis (MCDA)
by: Alberto Jiménez, et al.
Published: (2018-12-01)

A Methodology for the Selection of Multi-Criteria Decision Analysis Methods in Real Estate and Land Management Processes
by: Maria Rosaria Guarini, et al.
Published: (2018-02-01)

Evaluating health policy and legal responses : how to reduce barriers and improve access to orphan drugs for rare diseases in Canada
by: Blais, Catherine-Marie
Published: (2016)

Public Initiatives of Settlement Transformation: A Theoretical-Methodological Approach to Selecting Tools of Multi-Criteria Decision Analysis
by: Maria Rosaria Guarini, et al.
Published: (2017-12-01)

A multi-stakeholder multicriteria decision analysis for the reimbursement of orphan drugs (FinMHU-MCDA study)
by: Fernando de Andrés-Nogales, et al.
Published: (2021-04-01)

Are MCDA Methods Benchmarkable? A Comparative Study of TOPSIS, VIKOR, COPRAS, and PROMETHEE II Methods
by: Wojciech Sałabun, et al.
Published: (2020-09-01)

European and Italian regulation on orphan medicinal products
by: Roberta Joppi
Published: (2013-03-01)

Using a stated preference discrete choice experiment to assess societal value from the perspective of patients with rare diseases in Italy
by: Julio López-Bastida, et al.
Published: (2019-06-01)

A MCDA MODEL FOR OLIVE OIL SUPPLIER SELECTION USING MACBETH
by: Teresa Pereira, et al.
Published: (2019-12-01)

Reimbursement Status and Recommendations Related to Orphan Drugs in European Countries
by: Ewa Stawowczyk, et al.
Published: (2019-11-01)

ELECTRE ME: a proposal of an outranking modeling in situations with several evaluators
by: Helder Gomes Costa, et al.
Published: (2018-11-01)

Generating criteria for the decision-making process using geoprocessing techniques
by: Paulo Roberto Fitz, et al.
Published: (2007-01-01)

THE USE OF MULTI-CRITERIAL DECISION ANALYSIS (MCDA) FOR ESTIMATING THE THERAPEUTIC VALUE OF INNOVATIVE DRUGS
by: V. K. Fedyaeva, et al.
Published: (2017-08-01)

Efficiency of Methods for Determining the Relevance of Criteria in Sustainable Transport Problems: A Comparative Case Study
by: Andrii Shekhovtsov, et al.
Published: (2020-09-01)

Analysis of patient access to orphan drugs in Turkey
by: Güvenç Koçkaya, et al.
Published: (2021-02-01)

A multi-criteria approach to the evaluation of food safety interventions.
by: Dunn, Alexander Hiram
Published: (2015)

Setting health sector priorities: a brief overview of Ethiopia’s experience
by: Mahlet Kifle Habtemariam, et al.
Published: (2018-11-01)

Including the public perspective in health-related MCDA: ideas from the field of public opinion research and polling
by: Gillian K. SteelFisher
Published: (2018-11-01)

A New Decision Model Approach for Health Technology Assessment and A Case Study for Dialysis Alternatives in Turkey
by: Necla Öztürk, et al.
Published: (2020-05-01)

An analysis of orphan medicine expenditure in Europe: is it sustainable?
by: Jorge Mestre-Ferrandiz, et al.
Published: (2019-12-01)

Do payers value rarity? An analysis of the relationship between disease rarity and orphan drug prices in Europe
by: Goran Medic, et al.
Published: (2017-01-01)

Off-label use of orphan medicinal products: a Belgian qualitative study
by: Marc Dooms, et al.
Published: (2016-10-01)

Current Problems in Provision of Orphan Drugs and Ways to Solve Them
by: Alexei S. Kolbin, et al.
Published: (2016-09-01)

Estimating the clinical cost of drug development for orphan versus non-orphan drugs
by: Kavisha Jayasundara, et al.
Published: (2019-01-01)

How to assess urban quality: a spatial multicriteria decision analysis approach [Come valutare la qualità urbana: un approccio di analisi decisionale spaziale multi-criteriale per gli spazi aperti pubblici]
by: Alessandra Oppio, et al.
Published: (2021-07-01)

Panel discussion on the application of MCDA tools
by: Michael Watson
Published: (2018-11-01)

A systematic review of moral reasons on orphan drug reimbursement
by: Bettina M. Zimmermann, et al.
Published: (2021-06-01)

Renewable Energy Problems: Exploring the Methods to Support the Decision-Making Process
by: Paula Donaduzzi Rigo, et al.
Published: (2020-12-01)

Green Energy for a Green City—A Multi-Perspective Model Approach
by: Jarosław Wątróbski, et al.
Published: (2016-07-01)

Methodological approaches to the assessment of orphan medicinal products when making decisions about their inclusion in the program of medicinal maintenance: international experience and possible ways of its adaptation to the conditions of the health care system of the russian federation
by: N. G. Goloenko, et al.
Published: (2018-02-01)

Methodological Quality Assessment of Budget Impact Analyses for Orphan Drugs: A Systematic Review
by: Khadidja Abdallah, et al.
Published: (2021-04-01)

Multiple-criteria decision analysis process by using prospect decision theory in interval-valued neutrosophic environment
by: Chinnadurai Veerappan, et al.
Published: (2020-05-01)

Cannot write session to /tmp/vufind_sessions/sess_5v9sna8b3m6atk3d1lptfkvh33