“Growth patterns in children with mucopolysaccharidosis type I-Hurler after hematopoietic stem cell transplantation: Comparison with untreated patients”
The impact of hematopoietic stem cell transplantation (HSCT) on growth in patients diagnosed with mucopolysaccharidosis I Hurler (MPS-IH) has been historically regarded as unsatisfactory. Nevertheless, the growth patterns recorded in transplanted patients have always been compared to those of health...
Main Authors: | Alessandro Cattoni, Sofia Chiaraluce, Serena Gasperini, Silvia Molinari, Andrea Biondi, Attilio Rovelli, Rossella Parini |
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Format: | Article |
Language: | English |
Published: |
Elsevier
2021-09-01
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Series: | Molecular Genetics and Metabolism Reports |
Subjects: | |
Online Access: | http://www.sciencedirect.com/science/article/pii/S2214426921000811 |
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