RNA Trans-Splicing Modulation via Antisense Molecule Interference
In recent years, RNA trans-splicing has emerged as a suitable RNA editing tool for the specific replacement of mutated gene regions at the pre-mRNA level. Although the technology has been successfully applied for the restoration of protein function in various genetic diseases, a higher trans-splicin...
Main Authors: | Bernadette Liemberger, Josefina Piñón Hofbauer, Verena Wally, Claudia Arzt, Stefan Hainzl, Thomas Kocher, Eva M. Murauer, Johann W. Bauer, Julia Reichelt, Ulrich Koller |
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Format: | Article |
Language: | English |
Published: |
MDPI AG
2018-03-01
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Series: | International Journal of Molecular Sciences |
Subjects: | |
Online Access: | http://www.mdpi.com/1422-0067/19/3/762 |
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