A role for adeno-associated viral vectors in gene therapy

A role for adeno-associated viral vectors in gene therapy

Gene therapy constitutes a therapeutic intervention based on modification of the genetic material of living cells, by correcting genetic defects or overexpressing therapeutic proteins. The success of gene therapy protocols depends on the availability of therapeutically suitable genes, appropriate ge...

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Bibliographic Details
Main Authors:	Renata dos Santos Coura, Nance Beyer Nardi
Format:	Article
Language:	English
Published:	Sociedade Brasileira de Genética 2008-01-01
Series:	Genetics and Molecular Biology
Subjects:	Adeno-associated virus AAV-based recombinant vectors gene therapy
Online Access:	http://www.scielo.br/scielo.php?script=sci_arttext&pid=S1415-47572008000100001

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