Characterisation of lentiviral transgene expression in muscle precursor cells : towards a potential therapy for Duchenne Muscular Dystrophy
Duchenne Muscular Dystrophy is an X-linked genetic disorder characterised by progressive muscle degeneration due to the absence of functional dystrophin protein. Damaged muscle fibres are initially regenerated by satellite cells, the principal muscle-resident stem cells, which give rise to committed...
Main Author: | Jonuschies, J. |
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Published: |
University College London (University of London)
2012
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Subjects: | |
Online Access: | http://ethos.bl.uk/OrderDetails.do?uin=uk.bl.ethos.579499 |
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