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Clinical Pharmacokinetics and Pharmacodynamics of Cerliponase Alfa, Enzyme Replacement Therapy for CLN2 Disease by Intracerebroventricular Administration
by
Aryun Kim
,
Anita Grover
,
Kevin Hammon
,
Greg deHart
,
Peter Slasor
,
Anu Cherukuri
,
Temitayo Ajayi
,
David Jacoby
,
Angela Schulz
,
Nicola Specchio
,
Emily deLos Reyes
,
Paul Gissen
,
Joshua W. Henshaw
Published 2021-03-01
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Angela Schulz
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Anita Grover
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Anu Cherukuri
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David Jacoby
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1
Greg deHart
1
Joshua W. Henshaw
1
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