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Genetic Therapy
Humans
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gene therapy
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human
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genetics
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procedures
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Anemia, Hemolytic, Congenital Nonspherocytic
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CD34 antigen
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DNA Methylation
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DNA methylation
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Gene Expression
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HS-5 cell line
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History, 21st Century
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MDS
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PKLR gene
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1by Barcellini, W., Bianchi, P., Glader, B., Grace, R.F, López Lorenzo, J.L, Navarro Ordoñez, S., Nicoletti, E., Schwartz, J.D, Segovia, J.C, Sevilla, J., Shah, A.J, Zanella, A.View Fulltext in Publisher
Published 2022
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3by Alley, S.C, Bateman, K., Beaver, C.J, Boer, J., Buonarati, M., Dandamudi, S., Dasgupta, A., Dean, B., Dillen, L., Edmison, A., Elliott, R., Evans, C., Fandozzi, C., Faustino, P., Ferrari, L., Fraier, D., Garofolo, F., Gorovits, B., Haidar, S., Hughes, N., Ji, A., Jian, W., Lee, A., Li, W., Lima Santos, G.M, Luo, L., McGuinness, M., Mirza, T., Mylott, B., Neubert, H., Nouri, P., Olah, T., Post, N., Qian, M., Savoie, N., Shakleya, D., Spellman, D.S, Sporring, S., Stojdl, S., Summerfield, S., Sundman, P., Sydor, J., Tampal, N., Vinter, S., Voelker, T., Wang, J., Welink, J., Wilson, A., Woolf, E., Wu, J., Yang, E., Yu, H., Zhang, H., Zhang, J., Zhang, J.View Fulltext in Publisher
Published 2021
Article