Challenges associated with homologous directed repair using CRISPR-Cas9 and TALEN to edit the DMD genetic mutation in canine Duchenne muscular dystrophy.

by Sara Mata López, Cynthia Balog-Alvarez, Stanislav Vitha, Amanda K Bettis, Emily H Canessa, Joe N Kornegay, Peter P Nghiem
Published 2020-01-01

Correction: Challenges associated with homologous directed repair using CRISPR-Cas9 and TALEN to edit the DMD genetic mutation in canine Duchenne muscular dystrophy.

by Sara Mata López, Cynthia Balog-Alvarez, Stanislav Vitha, Amanda K Bettis, Emily H Canessa, Joe N Kornegay, Peter P Nghiem
Published 2020-01-01

Short-term treatment of golden retriever muscular dystrophy (GRMD) dogs with rAAVrh74.MHCK7.GALGT2 induces muscle glycosylation and utrophin expression but has no significant effec...

by Paul T Martin, Deborah A Zygmunt, Anna Ashbrook, Sonia Hamilton, Davin Packer, Sharla M Birch, Amanda K Bettis, Cynthia J Balog-Alvarez, Lee-Jae Guo, Peter P Nghiem, Joe N Kornegay
Published 2021-01-01

Oxidative damage to urinary proteins from the GRMD dog and mdx mouse as biomarkers of dystropathology in Duchenne muscular dystrophy.

by Jessica R Terrill, Basma A Al-Mshhdani, Marisa N Duong, Catherine D Wingate, Zahra Abbas, Angelo P Baustista, Amanda K Bettis, Cynthia J Balog-Alvarez, Joe N Kornegay, Peter P Nghiem, Miranda D Grounds, Peter G Arthur
Published 2020-01-01