Efficacy of pentosan polysulfate in in vitro models of lysosomal storage disorders: Fabry and Gaucher Disease.

by Andrea N Crivaro, Juan M Mucci, Constanza M Bondar, Maximiliano E Ormazabal, Romina Ceci, Calogera Simonaro, Paula A Rozenfeld
Published 2019-01-01

Growth Plate Pathology in the Mucopolysaccharidosis Type VI Rat Model—An Experimental and Computational Approach

by Johana M. Guevara-Morales, Michael Frohbergh, Hector Castro-Abril, Juan J. Vaca-González, Luis A. Barrera, Diego A. Garzón-Alvarado, Edward Schuchman, Calogera Simonaro
Published 2020-05-01