Development of the Fabry Disease Patient-Reported Outcome (FD-PRO): a new instrument to measure the symptoms and impacts of Fabry Disease

by Alaa Hamed, Pronabesh DasMahapatra, Nicole Lyn, Chad Gwaltney, Robert J. Hopkin
Published 2021-06-01

Development and psychometric validation of the Nausea/Vomiting Symptom Assessment patient-reported outcome (PRO) instrument for adults with secondary hyperparathyroidism

by Colleen A. McHorney, Mark E. Bensink, Laurie B. Burke, Vasily Belozeroff, Chad Gwaltney
Published 2018-02-01

Development and content validity of the Barth Syndrome Symptom Assessment (BTHS-SA) for adolescents and adults

by Chad Gwaltney, Jonathan Stokes, Anthony Aiudi, Iyar Mazar, Sarah Ollis, Emily Love, Alan Shields
Published 2021-06-01

Psychometric properties of the Japanese version of the Kansas City Cardiomyopathy Questionnaire in Japanese patients with chronic heart failure

by Emi Watanabe-Fujinuma, Hideki Origasa, Luke Bamber, Lothar Roessig, Tetsumi Toyoda, Yuri Haga, Chad Gwaltney, Burkert Pieske
Published 2020-07-01

Patient and caregiver perspectives on burden of disease manifestations in late-onset Tay-Sachs and Sandhoff diseases

by Nicole Lyn, Ruth Pulikottil-Jacob, Camille Rochmann, Robert Krupnick, Chad Gwaltney, Nick Stephens, Julie Kissell, Gerald F. Cox, Tanya Fischer, Alaa Hamed
Published 2020-04-01

Real-Life Multimarker Monitoring in Patients with Heart Failure: Continuous Remote Monitoring of Mobility and Patient-Reported Outcomes as Digital End Points in Future Heart-Failur...

by Frank Kramer, Javed Butler, Sanjiv J. Shah, Christian Jung, Savina Nodari, Stephan Rosenkranz, Michele Senni, Luke Bamber, Stephan Cichos, Chrysanthi Dori, Toeresin Karakoyun, Gabriele Jenny Köhler, Kinjal Patel, Paolo Piraino, Thomas Viethen, Praneeth Chennuru, Ayse Paydar, Jason Sims, Richard Clark, Rob van Lummel, Alexandra Müller, Chad Gwaltney, Salko Smajlovic, Hans-Dirk Düngen, Wilfried Dinh
Published 2020-06-01